Promoter-Targeted CRISPR Correction of PMP22 Gene Dosage Restores Schwann Cell Homeostasis in Charcot-Marie-Tooth Disease Type 1A.

Doo H M, Nam S H, Kim H, Lee K I, Young Lee J, Park S H, Kim Y J, Choi B-O, Kim J H

Tissue Eng Regen Med. 2026 Sep 27. PMID: 42801440. Abstract