European expert recommendations for comprehensive pre-treatment, treatment-phase and post-treatment care of patients with metachromatic leukodystrophy treated with autologous haematopoietic stem and progenitor cell gene therapy.
Laugwitz L, Fumagalli F, Wehner K, Martin P, Kern J, Kaiser N, Kehrer C, Launer T, Juengling P, Steiner-Wilke I, et al.
Eur J Paediatr Neurol. 2026 Jun 30; 63:46-59. PMID: 42431052.Abstract