Design of a regulated lentiviral vector for hematopoietic stem cell gene therapy of globoid cell leukodystrophy. Ungari S, Montepeloso A, Morena F, Cocchiarella F, Recchia A, Martino S, Gentner B, Naldini L, Biffi A Mol Ther Methods Clin Dev. 2015; 2:15038. Epub 2015 Oct 14. PMID: 26509184. Abstract CommentRecommendBookmarkWatch